Gene therapy research repairs nerve transport systems damaged by glaucoma and dementia: Results of the pre-clinical study, led by Professor Keith Martin from the Centre for Eye Research Australia and University of Melbourne and Dr Tasneem Khatib from the University of Cambridge, are published today in Science Advances. Researchers say the findings in experiments on mice show […]
A new dedicated gene therapy hub for the North of England will fast-track treatments for diseases and conditions which are at present incurable. The Gene Therapy Innovation and Manufacturing Centre (GTIMC) housed in Sheffield will be one of three cutting-edge hubs in the UK dedicated to advancing the training, capacity building and development of clinical […]
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Gene therapy research regenerates optic nerve, bringing hope for future glaucoma treatment: Researchers have used gene therapy to regenerate damaged optic nerve fibres in a discovery that could help treat glaucoma, one of the world’s leading causes of blindness. The pre-clinical study, led by Professor Keith Martin from the Centre for Eye Research Australia and […]
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My decision to get involved with developing gene therapy for neurological disorders came about because my own daughter, Ornella, 11, was born with a rare genetic condition known as Sanfilippo Syndrome, or mucopolysaccharidosis (MPS-IIIA). One in 70,000 babies is born with this life-limiting condition that results from a genetic mutation of a particular enzyme and […]